Importance of timely intervention

Duchenne muscular dystrophy (DMD) is caused by a mutation in the gene that codes for dystrophin – a protein that helps to keep muscles working properly.1

As a result, the body cannot make dystrophin and muscles weaken. Over time, this muscle weakness will lead to many health problems. Eventually, the muscles that control the heart and lungs stop working properly.2

The good news is that management and treatment options are available and can have a positive impact on the way DMD progresses.2 This includes medications as well as other interventions such as physiotherapy to help maintain muscles and joints.

Medications can help slow down loss of muscle function and weakness, which may help to delay complications. This means that your child or young person may stay mobile longer and live more independently and longer than they would without specialised care and management.1,3,4

Three ways appropriate management can help:1–4

number 1

May stop the disease progressing so rapidly

number 2

May help control symptoms

May help your child maintain their independence and quality of life for as long as possible

Talking to your doctor about the right treatment and management options is the most important step you can take. Learn more here

1. Birnkrant DJ, et al. Lancet Neurol. 2018;17:251–267 [Part 1].
2. Muscular Dystrophy Association. What is… Duchenne muscular dystrophy. Available at [last accessed March 2021].
3. Mah JK. Neuropsychiatr Dis Treat. 2016;12:1795–1807.
4. Gloss D, et al. Neurology. 2016;86:465–472.

Our Use of Cookies

In addition to cookies that are necessary to operate this website, we use optional cookies to provide website functionality and give you the best possible experience. We won't set optional cookies unless you enable them. For more detailed information see our Cookie Statement , which explains among others, how to set your cookie preferences and how to recall your consent.

Cookie Settings

Some cookies are essential, others help us improve your experience by providing insights into how the website is used. Select the cookie types listed below, and then save your preferences. Refer to our Cookie Statement for more information.

Strictly Necessary cookies
Strictly necessary cookies enable core functionality such as security, network management, and accessibility.

I accept the advertising/targeting cookies
Advertising/targeting cookies, which we use to track user activity and sessions so that we can deliver a more personalized service, and (in the case of advertising cookies) which are set by the third parties with whom we execute advertising campaigns and allow us to provide advertisements relevant to you.