Importance of timely intervention

Duchenne muscular dystrophy (DMD) is caused by a mutation in the gene that codes for dystrophin – a protein that helps to keep muscles working properly.1

As a result, the body cannot make dystrophin and muscles weaken. Over time, this muscle weakness will lead to many health problems. Eventually, the muscles that control the heart and lungs stop working properly.2

The good news is that management and treatment options are available and can have a positive impact on the way DMD progresses.2 This includes medications as well as other interventions such as physiotherapy to help maintain muscles and joints.

Medications can help slow down loss of muscle function and weakness, which may help to delay complications. This means that your child or young person may stay mobile longer and live more independently and longer than they would without specialised care and management.1,3,4

Three ways appropriate management can help:1–4

number 1

May stop the disease progressing so rapidly

number 2

May help control symptoms

May help your child maintain their independence and quality of life for as long as possible

Talking to your doctor about the right treatment and management options is the most important step you can take. Learn more here

1. Birnkrant DJ, et al. Lancet Neurol. 2018;17:251–267 [Part 1].
2. Muscular Dystrophy Association. What is… Duchenne muscular dystrophy. Available at https://www.mda.org/sites/default/files/2020/10/MDA_DMD_Fact_Sheet_Oct_2020.pdf [last accessed March 2021].
3. Mah JK. Neuropsychiatr Dis Treat. 2016;12:1795–1807.
4. Gloss D, et al. Neurology. 2016;86:465–472.

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